A new path forward for ultra-rare disease treatments Learn more Latest News News Source Blog May 14, 2026 ASGCT and Orphan Therapeutics Accelerator Launch CGTxchange -- A First-of-Its-Kind Marketplace to Reactivate Promising Shelved Cell and Gene Therapy Programs May 14, 2026 May 14, 2026 May 11, 2026 AGC Biologics Joins Orphan Therapeutics Accelerator’s Clinical Development Network as a Manufacturing Partner to Advance Cell and Gene Therapies for Ultra-Rare Diseases May 11, 2026 May 11, 2026 February 25, 2026 P4ML Becomes Founding Member of Orphan Therapeutics Accelerator (OTXL) to Support Broader Global Access to Ultra-Rare Disease Treatments February 25, 2026 February 25, 2026 View All News