Who We Are Founding Team and Advisors with vast experience in Rare Disease, GTx, Drug Development, Advocacy, Business, and Policy Leadership Team Craig MartinFounder & CEO Beth White, PhDCo-Founder & COO Deanna Portero, MPH, MBAVP, Partnerships & Innovation Gerald Cox, MD, PhD Chief Medical Officer Advisory Board Jim Geraghty Giacomo Chiesi Yael Weiss Sue Kahn Albert Seymour Tim Hunt Catherine Bollard Rich Gregory Robert Hesslein Amritha Jaishankar, PhD