Who We Are Founding Team and Advisors with vast experience in Rare Disease, GTx, Drug Development, Advocacy, Business, and Policy Leadership Team Craig MartinFounder & CEO Beth White, PhDCo-Founder & COO Deanna Portero, MPH, MBAVP, Partnerships & Innovation Gerald Cox, MD, PhDChief Medical Officer Advisory Board Jim Geraghty Giacomo Chiesi Yael Weiss Sue Kahn Albert Seymour Tim Hunt Catherine Bollard Rich Gregory Robert Hesslein Amritha Jaishankar, PhD